Combination intrathecal and intravenous gene therapy reveals a dominant role for treatment age in determining survival and behavioral outcomes in the mouse model of infantile neuronal ceroid lipofuscinosis
Lykken, Erik A., Rozenberg, Alejandra J., Gray, Steven J.Volume:
129
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2019.11.265
Date:
February, 2020
File:
PDF, 320 KB
2020