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High-Level Globin Gene Expression Mediated by a Recombinant Adeno-Associated Virus Genome That Contains the 3Ⲡγ Globin Gene Regulatory Element and Integrates as Tandem Copies in Erythroid Cells
Hargrove, Phillip W., Vanin, Elio F., Kurtzman, Gary J., Nienhuis, Arthur W.Volume:
89
Journal:
Blood
DOI:
10.1182/blood.v89.6.2167
Date:
March, 1997
File:
PDF, 652 KB
1997