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Intracerebroventricular cerliponase alfa for CLN2 disease: Clinical practice considerations from US clinics
Reyes, Emily de los, Lehwald, Lenora, Augustine, Erika F., Berry-Kravis, Elizabeth, Butler, Karen, Cormier, Natalie, Demarest, Scott, Lu, Sam, Madden, Jacqueline, Olaya, Joffre, See, Susan, Vierhile,Journal:
Pediatric Neurology
DOI:
10.1016/j.pediatrneurol.2020.04.018
Date:
May, 2020
File:
PDF, 873 KB
2020