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A helper-dependent adenoviral vector rescues CFTR to wild type functional levels in CF epithelial cells harbouring class I mutations
Cao, Huibi, Ouyang, Hong, Laselva, Onofrio, Bartlett, Claire, Zhou, Zhichang Peter, Duan, Cathleen, Gunawardena, Tarini, Avolio, Julie, Bear, Christine E., Gonska, Tanja, Hu, Jim, Moraes, Theo J.Journal:
European Respiratory Journal
DOI:
10.1183/13993003.00205-2020
Date:
May, 2020
File:
PDF, 1.98 MB
2020