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Treatment of infantile neuroaxonal dystrophy with RT001: A di-deuterated ethyl ester of linoleic acid: Report of two cases
Adams, Darius, Midei, Mark, Dastgir, Jahannaz, Flora, Christina, Molinari, Robert J, Heerinckx, Frederic, Endemann, Sarah, Atwal, Paldeep, Milner, Peter, Shchepinov, Mikhail S.Journal:
JIMD Reports
DOI:
10.1002/jmd2.12116
Date:
March, 2020
File:
PDF, 1.69 MB
2020