Gene therapy using a novel G6PC-S298C variant enhances the long-term efficacy for treating glycogen storage disease type Ia
Zhang, Lisa, Lee, Cheol, Arnaoutova, Irina, Anduaga, Javier, Starost, Matthew F., Mansfield, Brian C., Chou, Janice Y.Volume:
527
Journal:
Biochemical and Biophysical Research Communications
DOI:
10.1016/j.bbrc.2020.04.124
Date:
June, 2020
File:
PDF, 2.16 MB
2020