![](/img/cover-not-exists.png)
βT87Q-Globin Gene Therapy Reduces Sickle Hemoglobin Production, Allowing for Ex Vivo Anti-sickling Activity in Human Erythroid Cells
Demirci, Selami, Gudmundsdottir, Bjorg, Li, Quan, Haro-Mora, Juan J., Nassehi, Tina, Drysdale, Claire, Yapundich, Morgan, Gamer, Jackson, Seifuddin, Fayaz, Tisdale, John F., Uchida, NaoyaVolume:
17
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2020.04.013
Date:
June, 2020
File:
PDF, 2.07 MB
2020