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Early enzyme replacement therapy in Wolman disease: Challenges and outcomes
Aquino, Marcela B., Borges, Marcella S., Lopes, Isabela F., Vagnini, Laura, Fonseca, Jacqueline H.R., Carneiro, Zumira A., Lourenco, Charles M.Volume:
129
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2019.11.027
Date:
February, 2020
File:
PDF, 329 KB
2020