Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair
Ababneh, Nidaa A, Scaber, Jakub, Flynn, Rowan, Douglas, Andrew, Barbagallo, Paola, Candalija, Ana, Turner, Martin R, Sims, David, Dafinca, Ruxandra, Cowley, Sally A, Talbot, KevinJournal:
Human Molecular Genetics
DOI:
10.1093/hmg/ddaa106
Date:
June, 2020
File:
PDF, 1.93 MB
2020