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Gene therapy targeting the inner retina rescues the retinal phenotype in a mouse model of CLN3 Batten disease
kleine Holthaus, Sophia-Martha, Aristorena, Mikel, Maswood, Ryea, Semenyuk, Olha, Hoke, Justin, Hare, Aura, Smith, Alexander J, Mole, Sara E, Ali, Robin RJournal:
Human Gene Therapy
DOI:
10.1089/hum.2020.038
Date:
June, 2020
File:
PDF, 1.59 MB
2020