![](/img/cover-not-exists.png)
Phase 1â2 Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS
Miller, Timothy, Cudkowicz, Merit, Shaw, Pamela J., Andersen, Peter M., Atassi, Nazem, Bucelli, Robert C., Genge, Angela, Glass, Jonathan, Ladha, Shafeeq, Ludolph, Albert L., Maragakis, Nicholas J., MVolume:
383
Journal:
New England Journal of Medicine
DOI:
10.1056/NEJMoa2003715
Date:
July, 2020
File:
PDF, 917 KB
2020