Correction of both Tay-Sachs and Sandhoff diseases with the PS gene editing system
Ou, Li, Przybilla, Michael, TÄbÄran, Alexandru-Flaviu, Overn, Paula, O'Sullivan, Gerard, Jiang, Xuntian, Sidhu, Rohini, Kell, Pamela, Ory, Daniel, Whitley, Chester B.Volume:
129
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2019.11.326
Date:
February, 2020
File:
PDF, 323 KB
2020