Comparison of Organoid Swelling and in vivo Biomarkers of CFTR Function to Determine Effects of Lumacaftor-ivacaftor in Patients with Cystic Fibrosis Homozygous for the F508del Mutation
Graeber, Simon Y., van Mourik, Peter, Vonk, Annelotte M., Kruisselbrink, Evelien, Hirtz, Stephanie, van der Ent, Cornelis K, Mall, Marcus A, Beekman, Jeffrey MJournal:
American Journal of Respiratory and Critical Care Medicine
DOI:
10.1164/rccm.202004-1200le
Date:
July, 2020
File:
PDF, 352 KB
2020