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Development of the âHamburg best practice guidelines for ICV-enzyme replacement therapy (ERT) in CLN2 diseaseâ based on 5â¯years treatment experience in 48 patients
Schwering, Christoph, Wibbeler, Eva, Miriam, Nickel, Schulz, AngelaVolume:
129
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2019.11.385
Date:
February, 2020
File:
PDF, 324 KB
2020