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A novel approach to CNS dysfunction of Pompe disease with a fusion protein consisting of anti-transferrin receptor antibody and GAA enzyme
Tanaka, Satowa, Yoshioka, Aya, Kinoshita, Masafumi, Kida, Sachiho, Imakiire, Atsushi, Takenaka, Shinobu, Morimoto, Hideto, Yamamoto, Ryuji, Minami, Kohtaro, Sonoda, Hiroyuki, Takahashi, Kenichi, HiratVolume:
129
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2019.11.399
Date:
February, 2020
File:
PDF, 330 KB
2020