Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Sinha, Divya, Steyer, Benjamin, Shahi, Pawan K., Mueller, Katherine P., Valiauga, Rasa, Edwards, Kimberly L., Bacig, Cole, Steltzer, Stephanie S., Srinivasan, Sandhya, Abdeen, Amr, Cory, Evan, PeriyasJournal:
The American Journal of Human Genetics
DOI:
10.1016/j.ajhg.2020.06.011
Date:
July, 2020
File:
PDF, 6.68 MB
2020