Enzyme Replacement Therapy Can Reverse Pathogenic Cascade in Pompe Disease
Meena, Naresh Kumar, Ralston, Evelyn, Raben, Nina, Puertollano, RosaVolume:
18
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2020.05.026
Date:
September, 2020
File:
PDF, 3.20 MB
2020