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In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation
Moreno, Ana M., Fu, Xin, Zhu, Jie, Katrekar, Dhruva, Shih, Yu-Ru V., Marlett, John, Cabotaje, Jessica, Tat, Jasmine, Naughton, John, Lisowski, Leszek, Varghese, Shyni, Zhang, Kang, Mali, PrashantVolume:
28
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2020.06.027
Date:
August, 2020
File:
PDF, 87 KB
2020