[American Thoracic Society American Thoracic Society 2020 International Conference, May 15-20, 2020 - Philadelphia, PA - ()] C96. BEST OF PEDIATRICS - Onasemnogene Abeparvovec-xioi Gene-Replacement Therapy for Spinal Muscular Atrophy Type 1: Pulmonary and Ventilatory Findings from the Pivotal Phase 3 US Study (STR1VE)
Shell, R., Day, J.W., Chiriboga, C.A., Crawford, T.O., Darras, B.T., Finkel, R.S., Connolly, A.M., Iannaconne, S.T., Kuntz, N.L., Peña, L.D.M., Shieh, P.B., Smith, E.C., Kwon, J.M., Zaidman, C., SchuDOI:
10.1164/ajrccm-conference.2020.201.1_MeetingAbstracts.A5974
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