Benefits of Prophylactic Short-Course Immune Tolerance Induction in Patients With Infantile Pompe Disease: Demonstration of Long-Term Safety and Efficacy in an Expanded Cohort
Desai, Ankit K., Baloh, Carolyn H., Sleasman, John W., Rosenberg, Amy S., Kishnani, Priya S.Volume:
11
Journal:
Frontiers in Immunology
DOI:
10.3389/fimmu.2020.01727
Date:
August, 2020
File:
PDF, 719 KB
2020