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Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Campbell, Craig, Barohn, Richard J, Bertini, Enrico, Chabrol, Brigitte, Comi, Giacomo Pietro, Darras, Basil T, Finkel, Richard S, Flanigan, Kevin M, Goemans, Nathalie, Iannaccone, Susan T, Jones, KrisJournal:
Journal of Comparative Effectiveness Research
DOI:
10.2217/cer-2020-0095
Date:
August, 2020
File:
PDF, 1.09 MB
2020