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Early biochemical effects of velmanase alfa in a 7âmonthâold infant with alphaâmannosidosis
Santoro, Lucia, Zampini, Lucia, Padella, Lucia, Monachesi, Chiara, Zampieri, Stefania, Dardis, Andrea, Cordiali, Rosanna, Galeazzi, Tiziana, Catassi, CarloVolume:
55
Journal:
JIMD Reports
DOI:
10.1002/jmd2.12144
Date:
September, 2020
File:
PDF, 1.23 MB
2020