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Rescue of common exon skipping mutations in Cystic Fibrosis with modified U1 snRNAs
Stefano, Donegà , Rogalska, Malgorzata, Giulia, Pianigiani, Susana, Igreja, Margarida, Amaral Duarte, Franco, PaganiJournal:
Human Mutation
DOI:
10.1002/humu.24116
Date:
September, 2020
File:
PDF, 731 KB
2020