Generation of a gene edited hemophilia A patient-derived iPSC cell line, YCMi001-B-1, by targeted insertion of coagulation factor FVIII using CRISPR/Cas9
Sung, Jin Jea, Park, Sanghyun, Choi, Sang-Hwi, Kim, Jongwan, Cho, Myung Soo, Kim, Dong-WookVolume:
48
Journal:
Stem Cell Research
DOI:
10.1016/j.scr.2020.101948
Date:
October, 2020
File:
PDF, 1.51 MB
2020