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Assessment of plasma lyso-Gb3 for clinical monitoring of treatment response in migalastat-treated patients with Fabry disease
Bichet, Daniel G., Aerts, Johannes M., Auray-Blais, Christiane, Maruyama, Hiroki, Mehta, Atul B., Skuban, Nina, Krusinska, Eva, Schiffmann, RaphaelJournal:
Genetics in Medicine
DOI:
10.1038/s41436-020-00968-z
Date:
September, 2020
File:
PDF, 727 KB
2020