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014â AVXS-101 gene-replacement therapy (GRT) in presymptomatic spinal muscular atrophy (SMA): study update
Farrar, Michelle, Swoboda, Kathryn J, Schultz, Meredith, McMillan, Hugh, Parsons, Julie, Alexander, Ian E, Kernbauer, Elaine, Farrow, Marcia, Ogrinc, Francis G, Feltner, Douglas E, McGill, Bryan E, SpVolume:
90
Journal:
Journal of Neurology, Neurosurgery & Psychiatry
DOI:
10.1136/jnnp-2019-anzan.14
Date:
July, 2019
File:
PDF, 69 KB
2019