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Efficacy of adeno-associated virus gene therapy in a MNGIE murine model enhanced by chronic exposure to nucleosides
Vila-Julià , Ferran, Cabrera-Pérez, Raquel, Cámara, Yolanda, Molina-Berenguer, Miguel, Lope-Piedrafita, Silvia, Hirano, Michio, Mingozzi, Federico, Torres-Torronteras, Javier, MartÃ, RamonVolume:
62
Journal:
EBioMedicine
DOI:
10.1016/j.ebiom.2020.103133
Date:
December, 2020
File:
PDF, 2.83 MB
2020