Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2
Sondhi, Dolan, Kaminsky, Stephen M., Hackett, Neil R., Pagovich, Odelya E., Rosenberg, Jonathan B., De, Bishnu P., Chen, Alvin, Van de Graaf, Benjamin, Mezey, Jason G., Mammen, Grace W., Mancenido, DeVolume:
12
Journal:
Science Translational Medicine
DOI:
10.1126/scitranslmed.abb5413
Date:
December, 2020
File:
PDF, 888 KB
2020