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Volume 19; Issue 7

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Molecular Therapy
Volume 19; Issue 7

Molecular Therapy

Volume 19; Issue 7

1

Generation of a Kupffer Cell-evading Adenovirus for Systemic and Liver-directed Gene Transfer

Khare, Reeti, May, Shannon M, Vetrini, Francesco, Weaver, Eric A, Palmer, Donna, Rosewell, Amanda, Grove, Nathan, Ng, Philip, Barry, Michael A

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 708 KB

english, 2011

2

Single-particle Tracking as a Quantitative Microscopy-based Approach to Unravel Cell Entry Mechanisms of Viruses and Pharmaceutical Nanoparticles

Ruthardt, Nadia, Lamb, Don C, Bräuchle, Christoph

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 726 KB

english, 2011

3

Virally delivered Channelrhodopsin-2 Safely and Effectively Restores Visual Function in Multiple Mouse Models of Blindness

Doroudchi, M Mehdi, Greenberg, Kenneth P, Liu, Jianwen, Silka, Kimberly A, Boyden, Edward S, Lockridge, Jennifer A, Arman, A Cyrus, Janani, Ramesh, Boye, Shannon E, Boye, Sanford L, Gordon, Gabriel M,

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 811 KB

english, 2011

4

Nonredundant Roles of IL-10 and TGF-β in Suppression of Immune Responses to Hepatic AAV-Factor IX Gene Transfer

Hoffman, Brad E, Martino, Ashley T, Sack, Brandon K, Cao, Ou, Liao, Gongxian, Terhorst, Cox, Herzog, Roland W

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 387 KB

english, 2011

5

Late Abstracts: Presented at the American Society of Gene & Cell Therapy's 14th Annual Meeting, May 18–21, 2011, Seattle, Washington

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 239 KB

english, 2011

6

Switching on the Lights: The Use of Optogenetics to Advance Retinal Gene Therapy

Cronin, Therese, Bennett, Jean

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 366 KB

english, 2011

7

iPSCs: Unstable Origins?

Mukherjee, Sayandip, Thrasher, Adrian J

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 227 KB

english, 2011

8

Heartening Results: The CUPID Gene Therapy Trial for Heart Failure

Giacca, Mauro, Baker, Andrew H

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 203 KB

english, 2011

9

Pharmacological Characterization of Chemically Synthesized Monomeric phi29 pRNA Nanoparticles for Systemic Delivery

Abdelmawla, Sherine, Guo, Songchuan, Zhang, Limin, Pulukuri, Sai M, Patankar, Prithviraj, Conley, Patrick, Trebley, Joseph, Guo, Peixuan, Li, Qi-Xiang

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 500 KB

english, 2011

10

Nitric Oxide Synthase Gene Transfer Restores Activity of Circulating Angiogenic Cells From Patients With Coronary Artery Disease

Ward, Michael R, Thompson, Kathleen A, Isaac, Kathryn, Vecchiarelli, Jonathan, Zhang, Qiuwang, Stewart, Duncan J, Kutryk, Michael JB

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 586 KB

english, 2011

11

Rescue From Respiratory Dysfunction by Transduction of Full-length Dystrophin to Diaphragm via the Peritoneal Cavity in Utrophin/Dystrophin Double Knockout Mice

Ishizaki, Masatoshi, Maeda, Yasushi, Kawano, Ryoko, Suga, Tomohiro, Uchida, Yuji, Uchino, Katsuhisa, Yamashita, Satoshi, Kimura, En, Uchino, Makoto

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 411 KB

english, 2011

12

Pip5 Transduction Peptides Direct High Efficiency Oligonucleotide-mediated Dystrophin Exon Skipping in Heart and Phenotypic Correction in mdx Mice

Yin, HaiFang, Saleh, Amer F, Betts, Corinne, Camelliti, Patrizia, Seow, Yiqi, Ashraf, Shirin, Arzumanov, Andrey, Hammond, Suzan, Merritt, Thomas, Gait, Michael J, Wood, Matthew JA

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 1.05 MB

english, 2011

13

LiGluR Restores Visual Responses in Rodent Models of Inherited Blindness

Caporale, Natalia, Kolstad, Kathleen D, Lee, Trevor, Tochitsky, Ivan, Dalkara, Deniz, Trauner, Dirk, Kramer, Richard, Dan, Yang, Isacoff, Ehud Y, Flannery, John G

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 838 KB

english, 2011

14

Development of a Liver-specific Tet-On Inducible System for AAV Vectors and Its Application in the Treatment of Liver Cancer

Vanrell, Lucia, Di Scala, Marianna, Blanco, Laura, Otano, Itziar, Gil-Farina, Irene, Baldim, Victor, Paneda, Astrid, Berraondo, Pedro, Beattie, Stuart G, Chtarto, Abdelwahed, Tenenbaum, Lilianne, Prie

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 323 KB

english, 2011

15

Long-term Regulation of Genetically Modified Primary Hematopoietic Cells in Dogs

Okazuka, Kiyoshi, Beard, Brian C, Emery, David W, Schwarzwaelder, Kerstin, Spector, Michele R, Sale, George E, von Kalle, Christof, Kiem, Hans-Peter, Blau, C Anthony

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 361 KB

english, 2011

16

Feasibility of Adenovirus-Mediated hNIS Gene Transfer and 131I Radioiodine Therapy as a Definitive Treatment for Localized Prostate Cancer

Barton, Kenneth N, Stricker, Hans, Elshaikh, Mohamed A, Pegg, Jan, Cheng, Jingfang, Zhang, Yingshu, Karvelis, Kastytis C, Lu, Mei, Movsas, Benjamin, Freytag, Svend O

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 265 KB

english, 2011

17

Transcription Factor Rational Design Improves Directed Differentiation of Human Mesenchymal Stem Cells Into Skeletal Myocytes

Gonçalves, Manuel AFV, Janssen, Josephine M, Nguyen, Quynh G, Athanasopoulos, Takis, Hauschka, Stephen D, Dickson, George, de Vries, Antoine AF

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 906 KB

english, 2011

18

Imaging Stem Cell-derived Persistent Foci After In Vivo Selection of Lentiviral MGMT-P140K Transduced Murine Bone Marrow Cells

Lin, Yuan, Cheung, Perrin, Roth, Justin C, Wilson, David L, Gerson, Stanton L

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 1.06 MB

english, 2011

19

Shedding New Light on the Mechanism Underlying Stem Cell Therapy for the Heart

Mummery, Christine, Goumans, Marie Jose

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 387 KB

english, 2011

20

Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting

Tolar, Jakub, Adair, Jennifer E, Antoniou, Michael, Bartholomae, Cynthia C, Becker, Pamela S, Blazar, Bruce R, Bueren, Juan, Carroll, Thomas, Cavazzana-Calvo, Marina, Clapp, D Wade, Dalgleish, Robert,

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 155 KB

english, 2011

21

Secreted Antiviral Entry Inhibitory (SAVE) Peptides for Gene Therapy of HIV Infection

Egerer, Lisa, Volk, Andreas, Kahle, Joerg, Kimpel, Janine, Brauer, Frances, Hermann, Felix G, von Laer, Dorothee

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 261 KB

english, 2011

22

Distribution of Lentiviral Vector Integration Sites in Mice Following Therapeutic Gene Transfer to Treat β-thalassemia

Ronen, Keshet, Negre, Olivier, Roth, Shannah, Colomb, Charlotte, Malani, Nirav, Denaro, Maria, Brady, Troy, Fusil, Floriane, Gillet-Legrand, Beatrix, Hehir, Kathleen, Beuzard, Yves, Leboulch, Philippe

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 611 KB

english, 2011

23

Assembly of Therapeutic pRNA-siRNA Nanoparticles Using Bipartite Approach

Shu, Yi, Cinier, Mathieu, Fox, Sejal R, Ben-Johnathan, Nira, Guo, Peixuan

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 434 KB

english, 2011

24

In This Issue

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 1.32 MB

english, 2011

25

Research Highlights

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 680 KB

english, 2011

26

Late Abstracts: Presented at the American Society of Gene & Cell Therapy's 14th Annual Meeting, May 18–21, 2011, Seattle, Washington

Journal:

Molecular Therapy

Year:

2011

Language:

english

File:

PDF, 250 KB

english, 2011