Volume 25; Issue 2

Human Gene Therapy Clinical Development

Volume 25; Issue 2

1

Aerosol Delivery of DNA/Liposomes to the Lung for Cystic Fibrosis Gene Therapy

Davies, Lee A., Nunez-Alonso, Graciela A., McLachlan, Gerry, Hyde, Stephen C., Gill, Deborah R.

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 460 KB

english, 2014

2

Phase I/II Ex Vivo Gene Therapy Clinical Trial for Recessive Dystrophic Epidermolysis Bullosa Using Skin Equivalent Grafts Genetically Corrected with a COL7A1-Encoding SIN Retroviral Vector (GENEGRAFT)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 59 KB

english, 2014

3

Feasibility and Safety of Systemic rAAV9-h NAGLU Delivery for Treating Mucopolysaccharidosis IIIB: Toxicology, Biodistribution, and Immunological Assessments in Primates

Murrey, Darren A., Naughton, Bartholomew J., Duncan, F. Jason, Meadows, Aaron S., Ware, Tierra A., Campbell, Katie J., Bremer, William G., Walker, Christopher M., Goodchild, Laurie, Bolon, Brad, La Pe

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 981 KB

english, 2014

4

Fighting Blindness of Usher Syndrome: Diagnosis, Pathogenesis, and Retinal Treatment (TreatRetUsher) (TREATRUSH)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 46 KB

english, 2014

5

Optimization of Stem Cell Therapy for Clinical Trials of Degenerative Skin and Muscle Diseases (OptiStem)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 55 KB

english, 2014

6

Congratulations to the Winners of the 12 Pioneer Awards for Seminal Work in Gene and Cell Therapy

Journal:

Human Gene Therapy Clinical Development

Year:

2014

File:

PDF, 1.55 MB

2014

7

Introduction: Gene and Cell Therapy Projects of the Seventh Framework Program

Gancberg, David, Norstedt, Irene, Draghia-Akli, Ruxandra

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 32 KB

english, 2014

8

Persisting Transgenesis (PERSIST)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 54 KB

english, 2014

9

Advanced Cell-Based Therapies for the Treatment of Primary Immunodeficiency (Cell-PID)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 75 KB

english, 2014

10

Biodegradable Magnetic Stent for Coronary Artery Luminal Regeneration (Biomagscar)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 58 KB

english, 2014

11

Augmenting PBGD Expression in the Liver as a Novel Gene Therapy for Acute Intermittent Porphyria (AIPgene)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 57 KB

english, 2014

12

Gene-Activated Matrices for Bone and Cartilage Regeneration in Arthritis (GAMBA)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 60 KB

english, 2014

13

Therapeutic Challenge in Leukodystrophies: Translational and Ethical Research Toward Clinical Trials (LeukoTreat)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 55 KB

english, 2014

14

Pulsed Versus Continuous Application of the Prodrug 5-Fluorocytosine to Enhance the Oncolytic Effectiveness of a Measles Vaccine Virus Armed with a Suicide Gene

Yurttas, Can, Berchtold, Susanne, Malek, Nisar P., Bitzer, Michael, Lauer, Ulrich M.

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 1.20 MB

english, 2014

15

Nonhuman Adenovirus Vectors for Gene Transfer to the Brain (BrainCAV)

Journal:

Human Gene Therapy Clinical Development

Year:

2014

Language:

english

File:

PDF, 62 KB

english, 2014