Volume 16; Issue 8

Gene Therapy

Volume 16; Issue 8
1

Lentiviral vectors with amplified β cell-specific gene expression

Year:
2009
Language:
english
File:
PDF, 497 KB
english, 2009
3

Shortened ALK1 regulatory fragment maintains a specific activity in arteries feeding ischemic tissues

Year:
2009
Language:
english
File:
PDF, 715 KB
english, 2009
8

A muscle-targeting peptide displayed on AAV2 improves muscle tropism on systemic delivery

Year:
2009
Language:
english
File:
PDF, 322 KB
english, 2009
12

Translational stability for sickle gene therapy

Year:
2009
Language:
english
File:
PDF, 57 KB
english, 2009
13

Progress and Prospects: genetic treatments for disorders of bones and joints

Year:
2009
Language:
english
File:
PDF, 264 KB
english, 2009