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Volume 19; Issue 1
Main
Human Gene Therapy
Volume 19; Issue 1
Human Gene Therapy
Volume 19; Issue 1
1
Gene Therapy and Cement Injection for Restabilization of Loosened Hip Prostheses
de Poorter, Jolanda J.
,
Hoeben, Rob C.
,
Hogendoorn, Simone
,
Mautner, Vivien
,
Ellis, John
,
Obermann, Wim R.
,
Huizinga, Tom W.J.
,
Nelissen, Rob G.H.H.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 165 KB
Your tags:
english, 2008
2
Neonatal Intraperitoneal or Intravenous Injections of Recombinant Adeno-Associated Virus Type 8 Transduce Dorsal Root Ganglia and Lower Motor Neurons
Foust, Kevin D.
,
Poirier, Amy
,
Pacak, Christina A.
,
Mandel, Ronald J.
,
Flotte, Terence R.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 11.20 MB
Your tags:
english, 2008
3
Quantification and Characterization of Autotransduction in Retroviral Vector Producer Cells
Brandtner, Eva Maria
,
Kodajova, Petra
,
Knapp, Elzbieta
,
Ertl, Reinhard
,
Tabotta, Walter
,
Salmons, Brian
,
Günzburg, Walter H.
,
Hohenadl, Christine
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 161 KB
Your tags:
english, 2008
4
Advances in MicroRNAs: Implications for Gene Therapists
Marquez, Rebecca T.
,
McCaffrey, Anton P.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 258 KB
Your tags:
english, 2008
5
Adenovirus-Mediated Gene Delivery Rescues a Neonatal Lethal Murine Model of mut 0 Methylmalonic Acidemia
Chandler, Randy J.
,
Venditti, Charles P.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 209 KB
Your tags:
english, 2008
6
Protections for Participants in Gene Therapy Trials: A Patient's Perspective
Pattee, Suzanne R.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 35 KB
Your tags:
english, 2008
7
Informed Consent in Human Gene Transfer Clinical Trials
Kahn, Jeffrey
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 43 KB
Your tags:
english, 2008
8
Type II Pneumocyte-Restricted Green Fluorescent Protein Expression After Lentiviral Transduction of Lung Epithelial Cells
Wunderlich, Stephanie
,
Gruh, Ina
,
Winkler, Monica E.
,
Beier, Jennifer
,
Radtke, Kerstin
,
Schmiedl, Andreas
,
Groos, Stephanie
,
Haverich, Axel
,
Martin, Ulrich
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 685 KB
Your tags:
english, 2008
9
Future Meeting Dates for UK Department of Health: GTAC
Journal:
Human Gene Therapy
Year:
2008
File:
PDF, 27 KB
Your tags:
2008
10
Future Meeting Dates and Protocol Submission Deadlines for the RAC
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 22 KB
Your tags:
english, 2008
11
Human Gene Therapy, Consent, and the Realities of Clinical Research: Is It Time for a Research Subject Advocate?
Silber, Tomas Jose
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 49 KB
Your tags:
english, 2008
12
Prime Time for Small RNA-Based Therapeutics
Kay, Mark A.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 35 KB
Your tags:
english, 2008
13
Behind the Scenes of a Small RNA Gene-Silencing Pathway
Ku, Gregory
,
McManus, Michael T.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 518 KB
Your tags:
english, 2008
14
Induction of Transgene-Specific Cytotoxic T Lymphocyte Responses After Transplantation of Gene-Modified CD34 + Cells Despite Nonablative Immunosuppressive Conditioning
Piasecki, Julia C.
,
Beagles, Karen
,
Beard, Brian C.
,
Riddell, Stanley
,
Kiem, Hans-Peter
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 170 KB
Your tags:
english, 2008
15
Recombinant Adeno-Associated Virus-Mediated Global Anterograde Delivery of Glial Cell Line-Derived Neurotrophic Factor to the Spinal Cord: Comparison of Rubrospinal and Corticospinal Tracts in the Rat
Foust, Kevin D.
,
Flotte, Terence R.
,
Reier, Paul J.
,
Mandel, Ronald J.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 1.08 MB
Your tags:
english, 2008
16
Case of Leukaemia Associated with X-Linked Severe Combined Immunodeficiency Gene Therapy Trial in London
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 39 KB
Your tags:
english, 2008
17
Adverse Events in Gene Transfer Trials and an Agenda for the New Year
Wilson, James M.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 35 KB
Your tags:
english, 2008
18
If It's Broken, Shouldn't It Be Fixed? Informed Consent and Initial Clinical Trials of Gene Therapy
Caplan, Arthur L.
Journal:
Human Gene Therapy
Year:
2008
Language:
english
File:
PDF, 38 KB
Your tags:
english, 2008
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