![](/img/cover-not-exists.png)
Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe‐affected non‐human primates by intracerebral lentiviral gene therapy
Meneghini, Vasco, Lattanzi, Annalisa, Tiradani, Luigi, Bravo, Gabriele, Morena, Francesco, Sanvito, Francesca, Calabria, Andrea, Bringas, John, Fisher‐Perkins, Jeanne M, Dufour, Jason P, Baker, Kate CVolume:
8
Language:
english
Journal:
EMBO Molecular Medicine
DOI:
10.15252/emmm.201505850
Date:
May, 2016
File:
PDF, 3.87 MB
english, 2016